Initial AX-0810 data show no safety signals after 4 weeks of dosing and pharmacokinetics consistent with non-clinical data; ...
A1C, LDL, HDL… the number of medical abbreviations you might see on your patient portal is enough to make you think your ...
A UC San Diego lab recently announced a pair of scientific breakthroughs for Pitt-Hopkins and Rett syndromes that are slated ...
This study offers important insight into the pathogenic basis of intragenic frameshift deletions in the carboxy-terminal domain of MECP2, which account for some Rett syndrome cases, yet similar ...
Thirty-one years ago, Tomeka Cannon was so afraid that she called an ambulance as her eight-month-old daughter, Laneesha, had her first seizure. That initial, terrifying episode eventually progressed ...
Most days, 15-year-old Ella Frank lights up her family's living room with a quiet joy. Her fingernails are painted yellow, her hair clipped back with purple barrettes and small flower-shaped earrings ...
EXCLUSIVE: Magnolia Pictures will be opening its Toronto Film Festival acquisition Normal on April 17, 2026 in 2,000 theaters, the distributor’s widest release in its 24-year history. Normal, which we ...
Taysha Gene Therapies, Inc.’s lead asset is TSHA-102. This is an intrathecal AAV9 gene therapy for Rett with a 100% Phase 1/2 responder rate and favorable safety. The FDA granted it a Breakthrough ...
SPEIGLETOWN, N.Y. (NEWS10) — Families across the Capital Region came together on Saturday to raise money and awareness for a rare neurological disorder called Rett Syndrome. Saturday was the Reverse ...
TROY, N.Y. — A festival to bring attention to a severe neurological disorder will take place in Troy on Saturday. The Reverse Rett Upstate New York Fall Festival will take place from 11 a.m. to 5 p.m.
Mayor Gary McCarthy announced the sale of a long-vacant church at 535 Schenectady St. and an adjacent lot to Casale Investing LLC.According to the city, the co Columbia County family gives dog with ...
The TIFF-premiering neo-Western about an interim sheriff who senses something amiss about a small Minnesota town also stars Henry Winkler and Lena Headey. By Michael Rechtshaffen If there was any ...